Enthusiastic Parents Daunted by $740,000 Epilepsy Drug Price Tag
Parents of children with a rare type of epilepsy were hopeful when they heard about Ravicti, an FDA-approved drug that [...]
AmerisourceBergen Interview Highlights the Power of RWE in Drug Development Pipeline
A recent Fierce Biotech interview with AmerisourceBergen research experts focused on the role of real world evidence (RWE) in the [...]
ISPOR Webinar on Statistical Considerations in Rare Disease Research
The Professional Society for Health Economics and Outcomes Research (ISPOR) will hold a webinar on June 2nd at 1:00 PM [...]
AMCP Partnership Forum Discusses State of Rare Disease Outcomes and Research, Orphan Drugs to Hit $242 Billion by 2024
The AMCP (Academy of Managed Care Pharmacy) held a virtual meeting for healthcare professionals, payers, researchers, and pharma companies in [...]
Aurinia Announces ICER’s Favorable Review for Lupus Nephritis Drug
Aurinia Pharmaceuticals announced that ICER (the Institute for Clinical and Economic Review) has released a positive Evidence Report for its [...]
ICER to Investigate Treatments for Autoimmune Disease Myasthenia Gravis
ICER will determine the efficacy and economic outcomes of two treatments for autoimmune disease Myasthenia Gravis where neuromuscular junctions are [...]
Novartis and NHS England Agree on Price of Costly SMA Drug; Zolgensma Nearly £1.8 Million per Dose
SMA (spinal muscular atrophy) is characterized by muscle weakness, paralysis, and eventual loss of movement. It is associated with extremely [...]
Sarepta’s New Treatment for Duchenne Muscular Dystrophy Approved by FDA, $1 Million Yearly Cost Despite Lack of Confirmation Studies
Sarepta Therapeutics has created a third drug for use in Duchenne Muscular Dystrophy (DMD), termed Amondys 45. It recently received [...]
A Discussion with Paul Perreault of CSL Limited on COVID-19
Paul Perreault is CEO and Managing Director of CSL Limited, a top three global biotech company. He was invited to [...]
Will ‘All of Us’ Bring Positive Change to Research?
“All of Us” is the $1.5 billion initiative led by the federal government with the purpose of collecting health data from [...]