New gene therapies may soon treat dozens of rare diseases, but price tags will put them out of reach for many – Japan Today

New gene therapies may soon treat dozens of rare diseases, but price tags will put them out of reach for many Today 06:21 am JST By Kevin Doxzen TEMPE, Ariz
Zolgensma – which treats spinal muscular atrophy, a rare genetic disease that damages nerve cells, leading to muscle decay – is currently the most expensive drug in the world. A one-time treatment of the life-saving drug for a young child costs $2.1 million.

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2021-09-04 22:21:35